-
R.
Ziegler,
M.
Cherry,
Christine
Barbon,
Chester
Li,
S.
Bercury,
D.
Armentano,
R.
Desnick,
Seng
Cheng
(2007)
Correction of the biochemical and functional deficits in fabry mice following AAV8-mediated hepatic expression of alpha-galactosidase A.
Molecular therapy : the journal of the American Society of Gene Therapy, 15 3
-
Haiyan
Jiang,
L.
Couto,
Susannah
Patarroyo-White,
Tongyao
Liu,
D.
Nagy,
Joseph
Vargas,
Shangzhen
Zhou,
C.
Scallan,
J.
Sommer,
Sharmila
Vijay,
F.
Mingozzi,
K.
High,
G.
Pierce
(2006)
Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy.
Blood, 108 10
-
R.
Calcedo,
L.
Vandenberghe,
G.
Gao,
Jian-ping
Lin,
James
Wilson
(2009)
Worldwide epidemiology of neutralizing antibodies to adeno-associated viruses.
The Journal of infectious diseases, 199 3
-
S.
Parry,
J.
Holder,
M.
Halterman,
M.
Weitzman,
A.
Davis,
H.
Federoff,
rd
Strauss
(1998)
Transduction of human trophoblastic cells by replication-deficient recombinant viral vectors. Promoting cellular differentiation affects virus entry.
The American journal of pathology, 152 6
-
W.
Parks,
D.
Boucher,
J.
Melnick,
L.
Taber,
M.
Yow
(1970)
Seroepidemiological and Ecological Studies of the Adenovirus-Associated Satellite Viruses
Infection and Immunity, 2
-
StataCorp
(2009)
Stata statistical software: release 11
-
Lili
Wang,
R.
Calcedo,
Huan
Wang,
Peter
Bell,
R.
Grant,
L.
Vandenberghe,
Julio
Sanmiguel,
H.
Morizono,
M.
Batshaw,
James
Wilson
(2010)
The pleiotropic effects of natural AAV infections on liver-directed gene transfer in macaques.
Molecular therapy : the journal of the American Society of Gene Therapy, 18 1
-
Lili
Wang,
Joanita
Figueredo,
R.
Calcedo,
Jian-ping
Lin,
James
Wilson
(2007)
Cross-presentation of adeno-associated virus serotype 2 capsids activates cytotoxic T cells but does not render hepatocytes effective cytolytic targets.
Human gene therapy, 18 3
-
G.
Gao,
Mauricio
Alvira,
Lili
Wang,
R.
Calcedo,
J.
Johnston,
James
Wilson
(2002)
Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy
Proceedings of the National Academy of Sciences of the United States of America, 99
-
Baodong
Sun,
Haoyue
Zhang,
Luis
Franco,
S.
Young,
A.
Schneider,
A.
Bird,
A.
Amalfitano,
Y.-T.
Chen,
D.
Koeberl
(2005)
Efficacy of an adeno-associated virus 8-pseudotyped vector in glycogen storage disease type II.
Molecular therapy : the journal of the American Society of Gene Therapy, 11 1
-
R.
Sarkar,
R.
Tetreault,
G.
Gao,
Lili
Wang,
Peter
Bell,
R.
Chandler,
James
Wilson,
H.
Kazazian
(2004)
Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype.
Blood, 103 4
-
R.
Ziegler,
M.
Cherry,
Christine
Barbon,
Chester
Li,
S.
Bercury,
D.
Armentano,
R.
Desnick,
Seng
Cheng
(2007)
Correction of the Biochemical and Functional Deficits in Fabry Mice Following AAV8-mediated Hepatic Expression of α-galactosidase A.
Molecular therapy : the journal of the American Society of Gene Therapy, 15 3
-
M.
Friedman-Einat,
Z.
Grossman,
F.
Mileguir,
Z.
Smetana,
M.
Ashkenazi,
G.
Barkai,
N.
Varsano,
Eithan
Glick,
E.
Mendelson
(1997)
Detection of adeno-associated virus type 2 sequences in the human genital tract
Journal of Clinical Microbiology, 35
-
Lili
Wang,
R.
Calcedo,
Peter
Bell,
Jian-ping
Lin,
R.
Grant,
D.
Siegel,
James
Wilson
(2011)
Impact of pre-existing immunity on gene transfer to nonhuman primate liver with adeno-associated virus 8 vectors.
Human gene therapy, 22 11
-
A.
Davidoff,
J.
Gray,
C.
Ng,
Youbin
Zhang,
Junfang
Zhou,
Yunyu
Spence,
Yusura
Bakar,
A.
Nathwani
(2005)
Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models.
Molecular therapy : the journal of the American Society of Gene Therapy, 11 6
-
Tatiana
Burguete,
Michèle
Rabreau,
Marianne
Fontanges-Darriet,
Edith
Roset,
Hans-Dieter
Hager,
Alexandra
Köppel,
Paul
Bischof,
J.
Schlehofer
(1999)
Evidence for infection of the human embryo with adeno-associated virus in pregnancy.
Human reproduction, 14 9
-
G.
Hurlbut,
R.
Ziegler,
J.
Nietupski,
Joseph
Foley,
L.
Woodworth,
E.
Meyers,
S.
Bercury,
Nilesh
Pande,
D.
Souza,
M.
Bree,
M.
Lukason,
J.
Marshall,
Seng
Cheng,
R.
Scheule
(2010)
Preexisting immunity and low expression in primates highlight translational challenges for liver-directed AAV8-mediated gene therapy.
Molecular therapy : the journal of the American Society of Gene Therapy, 18 11
-
S.
Boutin,
Virginie
Monteilhet,
P.
Véron,
C.
Leborgne,
O.
Benveniste,
M.
Montus,
C.
Masurier
(2010)
Prevalence of serum IgG and neutralizing factors against adeno-associated virus (AAV) types 1, 2, 5, 6, 8, and 9 in the healthy population: implications for gene therapy using AAV vectors.
Human gene therapy, 21 6
-
C.
Walz,
T.
Anisi,
J.
Schlehofer,
L.
Gissmann,
A.
Schneider,
M.
Müller
(1998)
Detection of infectious adeno-associated virus particles in human cervical biopsies.
Virology, 247 1
-
L.
Vandenberghe,
Lili
Wang,
S.
Somanathan,
Yan
Zhi,
Joanita
Figueredo,
R.
Calcedo,
Julio
Sanmiguel,
Ravi
Desai,
Christopher
Chen,
J.
Johnston,
R.
Grant,
G.
Gao,
James
Wilson
(2006)
Heparin binding directs activation of T cells against adeno-associated virus serotype 2 capsid
Nature Medicine, 12